• Paediatric Precision Medicine

Translation of Paediatric Precision Medicine Clinical Trials – PPM 4a

Project Overview

The Clinical Trials project will underpin the translation ambition of the Paediatric Precision Medicine Program by building capacity to offer novel drugs and gene therapies to children with rare diseases and cancer.


  • Children’s Cancer Institute (Australia)
  • Children’s Medical Research Institute (Australia)
  • University of Sydney (Australia)
  • University of New South Wales (Australia)
  • Pharmaceutical/Biotechnology
  • Sydney Children’s Hospitals Network, Clinical Research Centre (Australia)

This project will leverage previous investments made by the New South Wales Government for world class infrastructure for the delivery of paediatric clinical trials. The project will provide additional resources to deliver novel drug and gene therapy clinical trials to children with rare genetics diseases and cancer.

Lead Investigators

  • Cate_Smith@2x

    Ms Cate Smith

    Associate Director Research Operations, Sydney Children’s Hospitals Network
  • Chris_Cowell@2x

    Professor Chris Cowell

    Director of Research, Sydney Children's Hospitals Network