Clinical Trials

Project Overview

The Clinical Trials project is at the core of the Paediatric Precision Medicine Program’s mission to translate groundbreaking therapies to children with rare diseases and cancer.

This initiative facilitated the execution of clinical trials involving novel gene and cell therapies for pediatric patients with rare genetic diseases and cancer. By prioritising children in trial design and development, the project significantly expanded the number of pediatric clinical trials in NSW.

Furthermore, it bolstered the capability of clinicians and researchers to identify potential trial opportunities, deepened their understanding of trial methodology and protocol design, and formulated an education, implementation, and service model to seamlessly deliver early-phase and innovative trials within the NSW healthcare system.


  • Children’s Cancer Institute (Australia)
  • Children’s Medical Research Institute (Australia)
  • University of Sydney (Australia)
  • University of New South Wales (Australia)
  • Pharmaceutical/Biotechnology
  • Sydney Children’s Hospitals Network, Clinical Research Centre (Australia)

The Clinical Trials program expanded the capabilities and resources for conducting innovative drug and gene therapy trials for children with rare genetic diseases and cancer, further enhancing investments in clinical trial infrastructure by the New South Wales Government.

Lead Investigators

  • LaniAttwoodPPM4a

    Ms Lani Attwood

    Advanced Therapeutics Program Manager, Kids Research, Sydney Children’s Hospitals Network
  • Chris_Cowell@2x

    Professor Chris Cowell

    Director of Research, Sydney Children's Hospitals Network


  • Professor Craig Munns

    Clinical Trials Lead, Sydney Children’s Hospital – Westmead
  • Dr Laura Fawcett

    Clinical Trials Lead, Sydney Children’s Hospital – Randwick
  • Amy Boland

    Clinical Trials Program Manager, Sydney Children’s Hospital Network